rare disease day 2017

PPD combines rare disease and pediatrics in new 'Center of Excellence'

By Melissa Fassbender

- Last updated on GMT

PPD announces Rare Disease and Pediatric Center of Excellence

Related tags Rare disease Epidemiology Medicine

The new center of excellence provides PPD clients with a team dedicated to clinical studies in rare disease and pediatric patient populations.

Pharmaceutical Product Development, LLC (PPD) announced the Rare Disease and Pediatric​ Center of Excellence on Rare Disease Day​, February 28th.

Karen Kaucic, M.D., PPD senior vice president will head the center of excellence out of the company’s Rockville, Maryland, office. The center’s 23 team members will be located at various PPD locations, along with six members of a steering committee.

According to the company, the team will be able to support end-to-end clinical trial solutions, including feasibility strategy, clinical information, biostatistics, pharmacovigilance, lab operations, and business analytics.

The center provides consultation on pre- and post-approval program and protocol development, innovative approaches to patient access and site management, strategies to address coordination of complex trial logistics, and application of customized patient-centric solutions to rare disease trial execution​,” Dr. Kaucic told us.

“Given that at least half of rare diseases touch children, we believe our approach of combining rare diseases and pediatrics within the center enables a more integrated approach to efficient delivery of rare disease programs​,” Dr. Kaucic added. “In addition, many of the patient-centric and customized approaches developed for rare diseases are highly relevant in pediatric clinical trial delivery more broadly​.” 

(Feature image: iStock/yacobchuk)

Related news

Show more

Related products

show more

The Right CDMO Can Unlock Faster Drug Development

The Right CDMO Can Unlock Faster Drug Development

Content provided by Lonza Small Molecules | 15-May-2023 | Interview

Drug development presents biotech companies with ever-changing challenges. Enabling a faster end-to-end process requires seamless flexibility and extensive...

SDTM supplemental qualifiers explained

SDTM supplemental qualifiers explained

Content provided by Formedix | 12-May-2023 | White Paper

What are SDTM supplemental qualifiers? In short, these are variables in non-CDISC datasets that cannot be mapped to a variable that matches the SDTM standard....

Plan for success with process liquid and buffer preparation

Plan for success with process liquid and buffer preparation

Content provided by Thermo Fisher Scientific - Process Liquid Preparation Services | 25-Apr-2023 | White Paper

Setting the groundwork for successful scale-up is essential for getting a therapeutic to market quickly and efficiently, but navigating the unknowns associated...

Related suppliers

Follow us


View more